A prenatal base-editing treatment that fixes a single DNA error in the SMN2 gene extended survival in SMA mice, a study found ...

But if you distill his message to its purest form, it is beautifully mundane: Performance capture might’ve saved his life, ...

Columnist Connie Chandler shares how a caregiver-patient relationship evolved into a friendship, where both women provide ...

In an interview-based study, adults with SMA reported a lack of coordination during their transition from pediatric care once ...

Columnist Connie Chandler writes of a generational disconnect with new SMA patients, but says living fully must remain their ...

Columnist Brianna Albers tends to make mountains out of molehills, a sure sign that living with SMA has resulted in illness anxiety.

Columnist Helen Baldwin worried the baby who arrived May 18, 1997, would keep everyone awake, but his silence signaled a ...

SMA Europe has launched an online tool designed to help patients, doctors, and others in the spinal muscular atrophy (SMA) ...

The exergame Tales from the Magic Keep aims to boost physical activity, and proved to be a feasible tool for children with ...

For people with spinal muscular atrophy, physical therapy can help support mobility, strength, and quality of life, regardless of SMA type.

“Come on, girl, just use your four extra arms!” I often tease my friends like this when we’re trying to accomplish a tricky caregiving task together. Some things would go a lot smoother if we had more ...

ARD-1676, a medication that works by tagging toxic proteins for destruction in cells, promotes clearance of the androgen receptor (AR) protein, which is faulty and clumps in spinal and bulbar muscular ...