Myotonic dystrophy type 1 (DM1) is the most common adult-onset form of muscular dystrophy and a condition that severely ...

Researchers at Baylor College of Medicine and their collaborators focused on Myotonic Dystrophy 1 heart problems testing a novel approach to restore normal function.

Dec. 10, 2024 — In a single IV injection, a gene therapy targeting cBIN1 can reverse the effects of heart failure and restore heart function in a large animal model. The therapy increases the ...

Researchers at the Kennedy Institute have developed a new computational framework that allows simultaneous analysis of gene expression and mechanical forces within cells and tissues, uncovering ...

A new study published in Cell Reports reveals a breakthrough discovery linking genetic variants in the gene ITSN1 to a significantly elevated risk of Parkinson's disease, a neurodegenerative condition ...

PCRX-201 became part of Pacira's portfolio in 2021, but was originally developed at Baylor and then by GQ Bio Therapeutics, ...

For example, scientists targeted a gene known as FGF5 (fibroblast growth factor 5), which targets the cycle of hair growth, creating longer, shaggy hair. They also altered the function of three ...

In an extraordinary achievement of advanced multiplexed genome engineering, Colossal Biosciences announces the birth of the Colossal Woolly Mouse—mice engineered to express multiple key mammoth-like ...

By combining three editing technologies, Colossal engineered mice that express multiple mammoth-identified traits relevant to cold adaptation.

It's not quite Jurassic Park, but so far, this is perhaps the closest humans have come yet to making the plot of that film a reality. This comes as Colossal Biosciences has reached a major ...

The journey to the woolly mouse began with the woolly mammoth. Scientists at Colossal examined more than 100 genomes of Asian ...