Bluebird Bio will sell itself to private equity firms Carlyle and SK Capital for about $30 million, the company said Friday.

An experimental trial of gene therapy has helped four toddlers - born with one of the most severe forms of childhood ...

Pfizer is pulling further away from the gene therapy field with its decision to discontinue hemophilia product Beqvez. | ...

Cardiac arrhythmias affect millions across the world and are responsible for a fifth of all deaths in the Netherlands.

A Connecticut boy is among four children all born with severe childhood blindness who gained “life-changing improvements” to ...

When the monkeys were single-celled embryos, scientists had used CRISPR editing tools to silence, or “knock out”, a gene that ...

According to multiple media reports on Thursday, Pfizer Inc. (NYSE:PFE) has terminated the global development and ...

At the Envision Summit 2025 in San Juan, Puerto Rico, Mike Farkas, MD, discussed gene therapy research for retinal ...

Scientists have identified a tiny genetic change—present in nearly all living humans but absent in our closest extinct ...

Researchers have identified a gene therapy that could prevent life-threatening arrhythmias by restoring the heart’s ...