The FDA approved betibeglogene autotemcel (beti-cel; Zynteglo) for adult and pediatric patients with transfusion-dependent ...

It means that eligible SCD patients in England now have access to the therapy following the prior agreement for transfusion-dependent beta thalassemia (TDT) patients announced last August. “Today is ...

This causes BCL11A to not be made which in turn allows gamma globin ... notably sickle cell disease and beta thalassemia. “Importantly it is also likely that making gamma globin is safe – it is our ...

It means that eligible SCD patients in England now have access to the therapy following the prior agreement for transfusion-dependent beta thalassemia (TDT) patients announced last August.

Vertex Pharmaceuticals (Nasdaq: VRTX) announced today a reimbursement agreement with NHS England for eligible sickle cell disease (SCD) patients to access the CRISPR/Cas9 gene-edited therapy, CASGEVY ...

Two mechanisms are responsible for iron overload in β-thalassemia: increased iron absorption due to ineffective erythropoiesis and blood transfusions. This review examines the mechanisms of myocardial ...

The Health Ministry (MoH) in cooperation with the Education Ministry (MoE) and Repsol Malaysia has launched a thalassemia awareness campaign, ‘NowyouSEEme’ for school students. Health Minister Datuk ...