Scientists have found a new way to stop cancer growth without damaging healthy cells. Researchers from the Francis Crick Institute and Vividion Therapeutics discovered a compound that blocks the ...
A 3-year-old girl who underwent a breakthrough gene therapy treatment to treat profound hearing loss can hear on her own, two ...
New research found that gene therapy for children with a form of severe combined immunodeficiency was successful in 95% of ...
A one-time gene therapy using a patient’s own stem cells has effectively cured a deadly immune disorder in 95% of treated ...
Researchers have unveiled a new DNA-based therapy that silences the PCSK9 gene to lower cholesterol without statin side effects. Early results show dramatic reductions in cholesterol levels, offering ...
An experimental gene therapy developed by researchers at UCLA, University College London and Great Ormond Street Hospital has ...
Musunuru provided ESGCT delegates with promising news of a roadmap following the diagnosis and treatment of Baby KJ.
Topline data showed that an investigational gene therapy slowed Huntington's disease progression and met its primary endpoint in a pivotal trial, uniQure Biopharma announced Wednesday. A high-dose ...
A new approach to gene therapy for retinitis pigmentosa may help patients with advanced disease regain vision regardless of which genetic mutation is causing the condition. An optogenetic therapy ...
To continue reading this content, please enable JavaScript in your browser settings and refresh this page. Preview this article 1 min The Cambridge biotech is working ...
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