Scientists have found a new way to stop cancer growth without damaging healthy cells. Researchers from the Francis Crick Institute and Vividion Therapeutics discovered a compound that blocks the ...
A 3-year-old girl who underwent a breakthrough gene therapy treatment to treat profound hearing loss can hear on her own, two ...
New research found that gene therapy for children with a form of severe combined immunodeficiency was successful in 95% of ...
A one-time gene therapy using a patient’s own stem cells has effectively cured a deadly immune disorder in 95% of treated ...
Researchers have unveiled a new DNA-based therapy that silences the PCSK9 gene to lower cholesterol without statin side ...
A study published in Science reveals a cellular mechanism involved in the inheritance of genetic mutations. The study also ...
Long-term follow-up shows 95% success rate, no serious complications in largest ADA-SCID gene therapy study to date ...