A new 3D human brain tissue platform developed by MIT researchers is the first to integrate all major brain cell types, ...
The world’s largest network of environmental groups approved the exploration of genetic engineering tools to aid in the ...
For children born with severe combined immunodeficiency due to adenosine deaminase deficiency (ADA-SCID), an investigational ...
The agency launched the Commissioner's National Priority Voucher pilot program to quickly approve products that could address national interests.
From the 2010s to the present, the existing technologies in the clinic and operating room have been improved with the goals ...
New research found that gene therapy for children with a form of severe combined immunodeficiency was successful in 95% of ...
A one-time gene therapy using a patient’s own stem cells has effectively cured a deadly immune disorder in 95% of treated ...
Patients with a very rare immune disorder who have gotten the gene therapy have experienced sustained long-term immune ...
Researchers have unveiled a new DNA-based therapy that silences the PCSK9 gene to lower cholesterol without statin side effects. Early results show dramatic reductions in cholesterol levels, offering ...
Sana Biotechnology, Inc. is working on a gene therapy to cure Type 1 diabetes. Click here to find out why SANA stock is a ...
A study published in Science reveals a cellular mechanism involved in the inheritance of genetic mutations. The study also ...
Long-term follow-up shows 95% success rate, no serious complications in largest ADA-SCID gene therapy study to date ...