Despite announcing a broad pivot to siRNA earlier this year, Sarepta is following through with an investigational gene ...

Smarter design through targeted delivery and human-relevant testing can save the industry from costly safety failures.

Researchers have unveiled a new DNA-based therapy that silences the PCSK9 gene to lower cholesterol without statin side effects. Early results show dramatic reductions in cholesterol levels, offering ...

A significant advance in treatment of patients with immunity to AAVs previously ineligible for clinical trials and existing ...

Significant advancements in gene silencing and gene editing offer new hope for treating rare disorders. Techniques like RNA ...

The gene therapy for neurological diseases market is poised for growth due to rising neurological disorder prevalence, demand ...

Endocrine therapy typically slows cell cycle progression by reducing cyclin D1, which partners with CDK4/6 to promote cell ...

Sana Biotechnology, Inc. is working on a gene therapy to cure Type 1 diabetes. Click here to find out why SANA stock is a ...

Researchers have understood for decades that some forms of deafness are inherited, yet until now, few of those genetic clues ...

From the 2010s to the present, the existing technologies in the clinic and operating room have been improved with the goals ...

Mercer County Community College launches an aseptic biomanufacturing program and mobile lab in Trenton to train students for ...