A single infusion of a CRISPR-based gene-editing therapy was associated with reductions in LDL cholesterol and triglycerides ...

University of Virginia School of Medicine researchers have used an advanced gene-editing technique to correct the underlying ...

University of Virginia School of Medicine scientists have used a next-generation form of gene editing to fix the underlying cause of a severe form of epilepsy in lab mice.

Preclinical testing has suggested that AIR-001 increases functional AAT protein levels and could address the lung and liver manifestations of the disease.

ChristianaCare Gene Editing Institute has received a $500,000 federal grant to expand its hands-on Learning Lab program, which introduces students to gene ...

Researchers at Cornell University have developed a powerful new genetic toolkit that allows scientists to study how genes ...

Doctors have never had so many cholesterol-lowering drugs at their disposal, but getting patients to take them every day is ...

Researchers have built a platform that programs short DNA fragments inside living cells to control protein activity, all ...

Researchers at Cornell University have developed a powerful new genetic toolkit that allows scientists to study how genes function at the level of ...

Treatment with the investigational base-editing gene therapy ristoglogene autogetemcel (risto-cel) showed promise in patients with sickle cell disease, according to an interim ana ...

A collaborative research study co-led by scientists at the Icahn School of Medicine at Mount Sinai and the Liber Institute for Brain Development has for the first time identified a biological process ...

Most people who have heard of clustered regularly interspaced short palindromic repeats (more commonly known as CRISPR) associate it with gene editing—the precise molecular scissors that allow ...