Shares of Sarepta Therapeutics SRPT plunged nearly 24% last week after the company reported the death of a patient following ...

Study results support the role of functional dystrophin and suggest that delandistrogene moxeparvovec stabilizes or slows ...

The death of a young boy with Duchenne muscular dystrophy (DMD ... therapy in boys aged two to three with the muscle-wasting disorder. As a precaution, Pfizer has now suspended dosing in a ...

DMD is a severe genetic disorder that causes muscle degeneration and weakness. Many people with this condition find their mobility declines significantly at an early age. Despite how DMD can ...

Scientists have been searching for ways to cure DMD for as long as they have known about the disease. Today, based on the wealth of knowledge about the underlying genetic and molecular mechanisms ...

and Geovanii – opportunities to explore California and Colorado are limited as they all are diagnosed with DMD, a progressive neuromuscular disorder. “Just being able to hang out with cousins ...

A comprehensive care approach can help people with ambulatory DMD maximize function and retain the ability to walk for as ...

If you’re living with Duchenne muscular dystrophy (DMD), planning ahead can help support the success of future education, employment, and housing efforts. Duchenne muscular dystrophy (DMD) is a ...

Duchenne Muscular Dystrophy (DMD) is a rare progressive disorder. People with DMD are missing muscle-protecting protein. This is due to a fault in the gene producing dystrophin. Muscles to become ...

DMD is an X-linked disorder characterized by progressive muscle weakness and wasting due to the absence of a protein called dystrophin, which in turn causes degeneration of skeletal and cardiac muscle ...

Italfarmaco S.p.A. today announced a comprehensive update on the regulatory and clinical advancements for givinostat, the company’s drug for the treat ...