Hosted on MSN1mon
Could a pill replace gene therapy for sickle cell disease? Research uncovers potential path to small-molecule drugIt does so by suppressing the gene BCL11A, which normally shuts down fetal hemoglobin production after birth. This lets fetal hemoglobin production resume. However, Casgevy and other gene ...
Results that may be inaccessible to you are currently showing.
Hide inaccessible results
Feedback