A recent review published in the journal Engineering delves into the significant advancements and potential of CRISPR ...

A new review in Engineering reveals that CRISPR technologies are revolutionizing regenerative medicine. Scientists from ...

Transformational drugs rarely emerge from a targeted, application-driven approach. Rather, they arise from deep scientific inquiry over many years, an approach that only robust, early-stage funding ...

Correspondence to Dr Minna Männikkö, Northern Finland Birth Cohort Studies, Faculty of Medicine, Aapistie 5 / P.O. Box 5000, 90014 University of Oulu, Finland; minna.ruddock{at}oulu.fi Background Low ...

― On track to provide clinical data from the 12 mg dose cohort from the Phase 1b PIONEER trial of pociredir in SCD in mid-2025 and the 20 mg dose cohort by the end of 2025 ― ― Ended 2024 with $241.0 ...

Erythropoiesis is a critical homeostatic process responsible for the production of red blood cells, essential for oxygen delivery to tissues. This review provides a brief overview of erythropoiesis: ...

Then, with help from Sankaran, patient samples from the National Institutes of Health, and a team in Sardinia, Italy, advances in genome-wide association studies revealed the gene that would hold the ...

Beginning with a landmark report in 2008, the lab published a series of studies that ultimately revealed the potential of editing one gene, BCL11A, with CRISPR/Cas9 technology to restore healthy ...

This technique allows for targeted editing of a specific regulatory enhancer segment of the BCL11A gene. Following this gene editing, patients undergo high-dose chemotherapy to clear their bone marrow ...

-More than 50 authorized treatment centers (ATCs) activated globally for CASGEVY, and more than 50 patients have had cells collected across all regions as of the end of 2024- -Clinical trials ...