In a report released yesterday, Tazeen Ahmad from Bank of America Securities maintained a Buy rating on Ultragenyx Pharmaceutical (RARE – ...

On a recent visit to Washington DC, Ho sat down with GEN Editorial Director Kevin Davies, PhD, to discuss Denali’s progress ...

Ultragenyx Pharmaceutical RARE announced that the European Commission (EC) has expanded the eligible patient population for ...

Data from the first patients enrolled into Regenxbio's trial of its gene therapy for rare inherited disease mucopolysaccharidosis type I (MPS I) – also known as Hurler syndrome – has shown the ...

In the largest study of its kind globally, UK clinicians and researchers at Royal Manchester Children’s Hospital (RMCH) part of Manchester University NHS Foundation Trust (MFT), and Great Ormond ...

Political leaders have shunned the Alternative for Germany. But on his social media platform X, Mr. Musk is pitching the party as mainstream. By Jim Tankersley Pierre Poilievre, the Conservative ...

After Donald Trump suggested he might take over Greenland by force, the consensus among the island’s population appears to be bewilderment and anxiety. By Jeffrey Gettleman and Maya Tekeli ...

Jan. 8, 2025 — Researchers have unearthed two fossils, named Punk and Emo, revealing that ancient molluscs were more complex and adaptable than previously ...

A state of emergency has been declared in Russia's western city of Engels, according to the region's governor. It comes after Ukraine said it was behind a drone strike on a Russian oil base in the ...

Fast-growing wildfires raging in Los Angeles killed at least two people on Wednesday, destroying hundreds of buildings, scorching hillsides and prompting officials to order some 70,000 people to ...

The Black Panthers’ work providing medical services to poor communities continues today in activism against the medical industrial complex’s ties to mass incarceration. Both sides in Sudan’s ...