A breakthrough in safely delivering therapeutic DNA to cells could transform treatment for millions suffering from common ...

June 13, 2024 — A viral gene therapy has reversed some brain abnormalities in infant mice with FOXG1 syndrome, a significant step toward one day treating children with this severe neurodevelopmental ...

ViroCell Biologics ("ViroCell" or the "Company"), a cell and gene therapy ("CGT") contract development and manufacturing organization ("CDMO") specializing in GMP viral vector manufacturing for ...

The death of a 16-year-old boy evokes a lengthy battle to realize the benefit of cutting-edge gene therapy while also ...

The therapy, EPI-321, is intended to treat cases of facioscapulohumeral muscular dystrophy, a genetic neuromuscular disorder.

With a storied history in vaccine development, India's Bharat Biotech is shaking things up and answering the call of advanced ...

In a groundbreaking advancement for families grappling with the challenges of Dravet syndrome, a rare and life-altering form ...

Our CGT facility is designed to produce high-titer viral vectors (AAV, Lentivirus, Adenovirus), which are essential for cell ...

The Company is currently analyzing the case and will update the prescribing information for Elevidys to note this development.

A breakthrough in safely delivering therapeutic DNA to cells using lipid nanoparticles could transform treatment for millions ...