A team of researchers from the San Raffaele-Telethon Institute for Gene Therapy (SR-TIGET, Milan), led by Nadia Coltella and ...

Gene therapy can improve hearing in children and adults with congenital deafness or severe hearing impairment, a new study ...

The Johns Hopkins team that conducted the new study had previously shown that the molecule of interest, an “antisense ...

Scientific organizations recently called for a 10-year ban on human germline editing. But will we ever be ready? And how ...

South Korea's trade minister Yeo Han-koo will visit the United States from June 22 to 27, the trade ministry said on Saturday ...

How can early decisions in cell and gene therapy clinical development impact downstream progress toward commercialization and patient access?

Alsheebani is one of the first adults in the world, and the first adult at the medical system, to be effectively cured of sickle cell disease using gene therapy. "The doctors kept assuring me that it ...

Three major gene and cell therapy organizations called for a global 10-year moratorium on heritable human genome editing, warning the technology remains too risky for clinical use. The joint statement ...

KJ Muldoon, a 10-month-old baby who sparked nationwide headlines after receiving a first-of-its kind gene-editing treatment, was released from the hospital this week. KJ has spent the majority of ...

The first human applications of gene therapy before birth are expected within the next decade, pending rigorous safety and ethical evaluations. This new era also brings new questions.

For now, most therapies target the body's somatic cells, not the germline—but as our tools improve, the possibility of heritable cures edges closer, raising hope and new ethical questions.

An international group of gene editing leaders has put out a call for a 10-year ban on heritable human genome editing (HHGE), extending a moratorium that was first proposed in the fallout of a ...