Germline gene therapy and somatic gene therapy are two quite different proposals, and the legitimate concerns and risks of the former should not be used to stall progress on the latter.

Scientific organizations recently called for a 10-year ban on human germline editing. But will we ever be ready? And how ...

In the first part of this series, we explored how early genetic screening and gene therapy transform the lives of newborns and their families. Now, we’re taking an even earlier step: treating ...

In this case, they used an innovative therapy designed to "quiet" the faulty gene, ... For now, most therapies target the body's somatic cells, not the germline—but as our tools improve, ...

How can early decisions in cell and gene therapy clinical development impact downstream progress toward commercialization and patient access?

A new study highlights a historic step in personalized medicine, utilizing CRISPR gene-editing technology for a ...

Discover which therapies are expected to grab the HER2-low cancers market share @ HER2-low Cancers Market Report The HER2-low ...

“Germline editing has very serious safety concerns that could have irreversible consequences,” said Bruce Levine, M.D., the Barbara and Edward Netter Professor in Cancer Gene Therapy at the University ...

According to the American Cancer Society, survivors of childhood cancer can face health problems later in their adult life. Many boys who undergo cancer treatment before puberty can lose the ability ...

UC San Diego scientists have created a gene therapy that goes beyond masking Alzheimer’s symptoms—it may actually restore ...

Gene therapy for sickle cell disease may help improve a major contributing factor to stroke risk in patients, reports a new ...