Gene therapy can improve hearing in children and adults with congenital deafness or severe hearing impairment, a new study ...

A team of researchers from the San Raffaele-Telethon Institute for Gene Therapy (SR-TIGET, Milan), led by Nadia Coltella and ...

Building blocks for flexible bioprocessing must also be easy to install and take little time to train operators.

A team of researchers from the San Raffaele-Telethon Institute for Gene Therapy (SR-TIGET, Milan), led by Nadia Coltella and ...

This is the first time such results have been achieved in both children and adult patients born with a specific type of ...

Gene therapy can improve hearing in children and adults with congenital deafness or severe hearing impairment, a new study ...

The pivotal trial for Neurogene's Rett syndrome gene therapy makes use of baseline controls and a rigorous endpoint that ...