Gene therapy can improve hearing in children and adults with congenital deafness or severe hearing impairment, a new study ...

Gene therapy for sickle cell disease may help improve a major contributing factor to stroke risk in patients, reports a new ...

A new gene therapy delivery device could let hospital pharmacies make personalized nanomedicines to order. This democratized ...

The pivotal trial for Neurogene's Rett syndrome gene therapy makes use of baseline controls and a rigorous endpoint that ...

The duration of expression of the gene Cdx2 is tightly regulated by a newly identified DNA sequence element called an “attenuator.” ...

Google's DeepMind launches AlphaGenome, an artificial intelligence model that predicts gene expression from DNA sequence.

Last month, a baby got the world’s first personalized gene-editing treatment. What will this mean for millions of others with ...

PanCAN Chief Scientific & Medical Officer Dr. Anna Berkenblit writes about the key takeaways from the ASCO 2025 Annual ...

The company said the therapy is the first allogenic therapy developed with its Tmod technology to be tested in humans.