A new 3D human brain tissue platform developed by MIT researchers is the first to integrate all major brain cell types, ...

The agency launched the Commissioner's National Priority Voucher pilot program to quickly approve products that could address national interests.

From the 2010s to the present, the existing technologies in the clinic and operating room have been improved with the goals ...

Patients with a very rare immune disorder who have gotten the gene therapy have experienced sustained long-term immune ...

Researchers have unveiled a new DNA-based therapy that silences the PCSK9 gene to lower cholesterol without statin side effects. Early results show dramatic reductions in cholesterol levels, offering ...

Sana Biotechnology, Inc. is working on a gene therapy to cure Type 1 diabetes. Click here to find out why SANA stock is a ...

Significant advancements in gene silencing and gene editing offer new hope for treating rare disorders. Techniques like RNA ...

Endocrine therapy typically slows cell cycle progression by reducing cyclin D1, which partners with CDK4/6 to promote cell ...

These results are what we hoped for when we first began developing this approach,' one researcher said. View on euronews ...

An experimental gene therapy developed by researchers at UCLA, University College London and Great Ormond Street Hospital has ...

Since 2019, MIT researchers have published a new concept called prime editing, which is more precise than regular CRISPR-Cas9 gene editing. As a result, it has fewer off-target effects and less chance ...

Despite announcing a broad pivot to siRNA earlier this year, Sarepta is following through with an investigational gene ...