Despite announcing a broad pivot to siRNA earlier this year, Sarepta is following through with an investigational gene ...

Researchers have unveiled a new DNA-based therapy that silences the PCSK9 gene to lower cholesterol without statin side effects. Early results show dramatic reductions in cholesterol levels, offering ...

Significant advancements in gene silencing and gene editing offer new hope for treating rare disorders. Techniques like RNA ...

Study results published in The New England Journal of Medicine show the therapy significantly improved hearing in nearly a ...

Endocrine therapy typically slows cell cycle progression by reducing cyclin D1, which partners with CDK4/6 to promote cell ...

From the 2010s to the present, the existing technologies in the clinic and operating room have been improved with the goals ...

Mercer County Community College launches an aseptic biomanufacturing program and mobile lab in Trenton to train students for ...

Researchers have understood for decades that some forms of deafness are inherited, yet until now, few of those genetic clues ...

Sana Biotechnology, Inc. is working on a gene therapy to cure Type 1 diabetes. Click here to find out why SANA stock is a ...

Engineers have created DIAL, a modular system that precisely sets and edits protein levels in synthetic gene circuits. By ...

Explore the impact of lysosomal lipid recycling in a rare multi-organ disorder linked to the SPNS1 gene mutations.

The Center of Excellence in Medical Genetics, Faculty of Medicine, Chulalongkorn University, has launched one of the worl ...