EAU CLAIRE, Wis. (WEAU) - Governor Tony Evers names May 23rd as International GM1 Gangliosidosis Awareness Day, with Altoona resident Lindsay Jackelen receiving a proclamation. Jackelen suffers from ...
The ganglioside GM1 acts as a lipid-based receptor for internalization and traffic of cholera toxin (CT), which is ultimately sorted to the endoplasmic reticulum of host cells. As with other acidic ...
LYS-GM101 is a gene therapy designed to replace the gene mutation and restore the production of the beta-galactosidase enzyme. The Food and Drug Administration (FDA) has granted Fast Track designation ...
PARIS--(BUSINESS WIRE)--Regulatory News: Lysogene (FR0013233475 – LYS) (Paris:LYS), a phase 3 gene therapy platform Company targeting central nervous system (CNS) diseases, announced today that the ...
YONGIN, South Korea--(BUSINESS WIRE)--GC Pharma (006280.KS) and Tottori University today announced a worldwide licensing and collaboration agreement for the orally administrable chaperone drug of GM1 ...
"Every single day that goes by, we are losing a little bit more of them," Kyle Harrison says of his two daughters, Kinley and Kennedy, who have GM1 gangliosidosis Joelle Goldstein is a Senior News ...