ChromaTan Inc. and Landmark Bio PBLLC have been awarded a grant from the National Institute for Innovation in Manufacturing ...

June 13, 2024 — A viral gene therapy has reversed some brain abnormalities in infant mice with FOXG1 syndrome, a significant step toward one day treating children with this severe neurodevelopmental ...

Sarepta Therapeutics said on Tuesday that a 16-year-old boy died from acute liver failure months after receiving the company's U.S-approved gene therapy for a rare muscular dystrophy. The patient ...

Development strategies designed to reduce the unknowns so that cell and gene therapy innovators can develop robust processes ...

NY resident Sebastien Beauzile was treated with a pioneering new gene therapy approach called Lyfgenia, curing his sickle ...

The small study in patients with a rare disorder that causes liver and lung damage showed the potential for precisely ...

After scoring tax abatements for a $100 million investment in The Woodlands last year, the company appears to be close to beginning the project.

In a preclinical study, researchers at Children's Hospital of Philadelphia (CHOP) demonstrated a novel gene therapy with ...

Pfizer is pulling further away from the gene therapy field with its decision to discontinue hemophilia product Beqvez. The New York pharma is ending global development and commercialization of ...

Researchers successfully use an adeno-associated viral vector to restore brain function ... paving the way for future gene therapy in patients. Study: Neonatal but not Juvenile Gene Therapy ...

Biotherapeutics announced promising preclinical results for its systemic RTNova platform. The platform has successfully delivered ...