As soon as the hemoglobin level drops, Thalassemia patients feel unwell, despite taking medicines. But as soon as they ...
NY resident Sebastien Beauzile was treated with a pioneering new gene therapy approach called Lyfgenia, curing his sickle ...
Similarly, some gene therapies, especially for blood disorders such as beta-thalassemia, require the harvesting of patients' blood stem cells, insertion of a therapeutic gene, and expansion of the ...
A single molecular switch is essential for blood stem cells to enter an activated, regenerative state in which they produce ...
Certain genotypes of α-thalassemia present with microcytosis ... of an RBC to be dyed by a variety of laboratory stains Red Blood Cell Indices Series of relationships characterizing erythrocytes ...
The Rutgers Cancer Institute recently became a designated gene therapy treatment center for sickle cell anemia and beta-thalassemia, joining a small group of medical centers that currently provide ...
Japan's Ono Pharmaceutical is handing over $280 million upfront to acquire Ionis Pharmaceuticals’ phase 2-stage antisense ...
Doctors harvest stem cells from the patient’s bone marrow and then send them off to a lab, where CRISPR is used to turn up the production of another, functional version of haemoglobin. This version is ...
India is known as the “Thalassemia capital of the world.” It has the highest number of patients with thalassemia major in the world. India has around 50 million (5 crore) carriers of the ß ...