A patient death in a CRISPR trial halts gene editing studies, raising critical safety questions. What this means for the ...

Impella, which J&J touts as the world’s smallest heart pump, has a range of devices used for various heart conditions. Lexeo ...

This virtual event is part of the Transforming Pediatric Healthcare series from U.S. News & World Report, developed with ...

An HIV-derived nucleoside therapy now treats rare genetic diseases by restoring mitochondrial DNA and improving muscle ...

By Karen Roman Biopharmaceutical company Medera Inc. said it completed patient enrollment for Cohort B of its clinical trial ...

Avista Therapeutics, a preclinical gene therapy company built on deep clinical, computational and gene therapy expertise, today announced the significant expansion of its gene therapy platform.

A preclinical study uncovered a new gene therapy that targets pain centers in the brain while eliminating the risk of ...

U.K. biotech Ikarovec has teamed up with VectorBuilder to work on an eye disease gene therapy that could be administered in a ...

A new treatment might just be hope for many people living with chronic pain. In a recent preclinical study, researchers ...

Qure N.V. (NASDAQ:QURE) surged around 15% in early trading on Friday after the company said it has secured a Type A meeting ...

A heart attack survivor is the first person to receive groundbreaking gene therapy which aims to prevent a major heart ...

Cell and gene therapy are revolutionary approaches to treating diseases at the molecular level. They involve the manipulation ...