Although cystic fibrosis is a single gene mutation, there are more than 1,000 different ways the CFTR gene can mutate in ...

By Deena Beasley (Reuters) -Gene therapy, with its offer of a possible cure for rare diseases like sickle cell, is losing ...

A pair of privately-held developers of editing-based therapies have some successes to show for their recent efforts to ...

A recent review published in the journal Engineering delves into the significant advancements and potential of CRISPR ...

The gene therapy world is in turmoil, but Arbor, armed with more than a billion dollars in partnerships and raises, is going forward.

Sebastien Beauzile, 21, has been cured of sickle cell anemia, according to his doctors at Cohen Children’s Medical Center.

A sickle cell gene therapy treatment has allowed a Long Island man to turn a chapter in his life. He was Sebastien Beauzile ...

CRISPR Therapeutics' stock faces challenges with slow Casgevy adoption and competition. See how CRSP stock remains a cautious ...

Aaron Scott, of Fayetteville, is the first in North Carolina to receive a new FDA-approved therapy which uses the patient's own cells to relieve the pain of sickle cell disease.

CRISPR uses gene-editing technology to modify or correct DNA sequences, providing an opportunity to treat genetic disorders.

But in December, Beauzile, 21, became the first person in New York State to be made symptom-free of sickle cell disease after undergoing Lyfgenia, a new type of gene therapy that uses stem cell ...

The small study in patients with a rare disorder that causes liver and lung damage showed the potential for precisely ...